Longitudinal natural history in young boys with Duchenne Muscular Dystrophy

Longitudinal natural history in young boys with Duchenne Muscular Dystrophy, Over the last decades several studies have reported natural history data in Duchenne muscular dystrophy (DMD) [1–6]. Most of the studies using functional scales have focused on boys assessed after the age of 5 years., Over the last decades several studies have reported natural history data in Duchenne muscular dystrophy (DMD) [1–6]. Most of the studies using functional scales have focused on boys assessed after the age of 5 years. This is partly due to the fact that the mean age at diagnosis is still around 4-5 years [7,8], and partly to the fact that the available tools, such as the North Star Ambulatory Assessment (NSAA) or the Motor Function measure (MFM), were validated for populations over 5 years of age [9–11]., admin,